October 27, 2015 Texas man can eat, drink again after surgery corrects rare condition that caused drastic weight loss Wayne Weaver had always maintained a steady weight throughout his life, so when he began dropping pounds in fall 2014, he knew something was wrong, CBS DFW reported.
October 27, 2015 Pennsylvania baby whose disease prompted improved newborn screenings dies The little Pennsylvania girl who inspired improved newborn screenings for a rare regenerative disorder has passed away, MyFoxPhilly.com reported.
October 27, 2015 3-month-old South Dakota twins battling same type of cancer Three-month-old Kenedi and Kendal Breyfogle share the same eye color, the same little noses, ears and mouths, and, in many of their photos, the same outfits.
October 27, 2015 Newly approved drug restores lung function in woman with life-threatening disease A young woman diagnosed with a hard-to-treat, rare lung disease has found an unexpected solution in the form of a drug originally designed to prevent organ rejection in kidney transplant patients.
October 27, 2015 GSK readies 'bubble boy' drug as big pharma bets on gene therapy GlaxoSmithKline is close to seeking European approval for a gene therapy drug to fight adenosine deaminase severe combined immune deficiency (ADA-SCID) in the latest sign of a renaissance in the technology to fix faulty genes.
October 27, 2015 Texas girl with rare genetic disorder raises $13G for hospital that helped her gain mobility When Addie Bryan was diagnosed with a rare genetic disorder at birth, doctors never thought she would be able to walk, much less run.
October 27, 2015 Woman who vomited 100 times a day has been cured A young woman plagued with a disease that caused her to vomit more than 100 times per day has finally been cured.
October 27, 2015 Georgia girl recovering after receiving life-saving bone marrow transplant from sister A Georgia 4 year old is recovering after receiving a life-saving bone marrow transplant from one of her three sisters.
October 27, 2015 Sister donates bone marrow to girl battling rare disease A 7-year-old Massachusetts girl is celebrating a week home with her family after undergoing a lifesaving bone marrow transplant which was made possible through her younger sister.
October 27, 2015 'Unicorn woman' appeals for help as rare condition causes horn-like growth A woman with an abnormal growth on her head that appears to be in the shape of a large horn has become known in her village as the “unicorn woman.”